University of California San Diego-led team has discovered that restoring a key cardiac protein called connexin‑43 in a mouse ...

Hydrocephalus is a life-threatening condition that occurs in about 1 in 1,000 newborns and is often treated with invasive ...

New nanomaterial passes the blood-brain barrier to reduce damaging inflammation after the most common form of stroke. When ...

Nine people with a rare genetic condition that causes life-threatening inflammatory reactions appear to have been cured, after taking part in the first trial of a new version of a CRISPR-based gene ...

Tenaya Therapeutics’ gene therapy for an inherited heart condition that can cause sudden death appears to be effective in mice, new data show. In a journal article published March 18 in Nature ...

Researchers have designed a new genetic therapy that could alleviate debilitating giant moles in a rare skin condition. Researchers at the Francis Crick Institute, UCL Great Ormond Street Institute ...

(Reuters) -Novo Nordisk said on Monday the U.S. Food and Drug Administration (FDA) had approved its therapy to treat a rare genetic condition that affects the kidneys. The once-monthly injection, to ...

A three-year-old boy has astounded doctors with his progress after becoming the first person in the world with his devastating disease to receive a ground-breaking gene therapy. Oliver Chu has a rare, ...

A collaboration between researchers at New York University’s Grossman School of Medicine and Rocket Pharmaceuticals has produced preclinical evidence that gene replacement therapy successfully halts ...

At Liv Hospital, specialists emphasize that stem cell therapy isn’t a one-size-fits-all solution. Instead, it is carefully indicated for specific diseases, patient profiles, and treatment ...

A Northeast Ohio guitarist couldn't play without pain until he discovered a non-invasive procedure using low-dose radiation therapy.