Medical Xpress on MSN12 天
Gene therapy developed for maple syrup urine disease shows promise
A study led by UMass Chan Medical School researchers has demonstrated that a gene therapy to correct a mutation that causes ...
Fierce Biotech8 天
Gene therapy prevents death, restores growth in mice and a calf with maple syrup urine disease
A one-time injection of a novel gene therapy was able to save mice and a newborn calf from succumbing to maple syrup urine ...
Gene therapy for maple syrup urine disease shows promise
New gene therapy for maple syrup urine disease shows promise in preventing deadly symptoms in cows and offers hope for patients.