In a case that was billed as profits versus patients, India’s Supreme Court dismissed a petition in which Roche sought to ...

Kaitlin Batley, MD, a pediatric neurologist at Children’s Health and assistant professor at UT Southwestern Medical Center, highlights recent advancements and ongoing clinical trials in the spinal ...

Gene therapy is linked to better nonmotor outcomes in spinal muscular atrophy type 1 compared to first-line nusinersen, new ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

The SMA treatment team also includes rehabilitation professionals such as respiratory, physical, occupational, and speech therapists. Rehabilitation treatment involves care related to positioning, ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact customerservice@slackinc.com. Back to Healio Topline results from a phase 3 clinical ...

The Key Spinal Muscular Atrophy Companies in the market include - Genentech, F. Hoffmann-La Roche, Scholar Rock, Biohaven/ Bristol-Myers Squibb, NMD Pharma, Novartis ...

In a closely watched case, Roche suffered a setback as a court said it would permit a generic version of its rare disease ...

Panelists discuss how the current spinal muscular atrophy (SMA) treatment landscape includes 3 options: gene therapy (onasemnogene abeparvovec [Zolgensma]) for younger patients and 2 splice modifiers ...

With this judgment, Natco Pharma can now sell the Spinal Muscular Atrophy treatment drug for ₹15,900 compared to the previous ...

This is six year old Emma Nowll and like so many kids her age. She is *** prankster. You can also call her. She hates it when I try to help her so um the best thing I can do for her is to just teach ...

Imagine a child born in a family with a rare disease, whose treatment would cost more than 17 crore for a single dose. The ...