Infants with presymptomatic spinal muscular atrophy who were treated with risdiplam had improved functional and survival outcomes. At 12 months, most treated infants were able to sit and stand ...
For people with spinal muscular atrophy, physical therapy can help support mobility, strength, and quality of life, regardless of SMA type.
Irish Mirror on MSN
'The fact it’s not being used is wrong': Parents issue plea to HSE over life-changing heel prick test
The parents of two boys born with a rare genetic disorder have demanded the rollout of a life-changing heel prick test – ...
Kaitlin Batley, MD, a pediatric neurologist at Children’s Health and assistant professor at UT Southwestern Medical Center, highlights why it’s important patients with spinal muscular atrophy stay in ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results