Learn what you need to do to have a fun, safe, and stress-free day at an amusement park when you have spinal muscular atrophy.

A trip to England with her friend of 30-plus years prompts columnist Connie Chandler to give thanks for kind friends who ...

Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...

Salanersen (BIIB115/ION306) is an antisense oligonucleotide (ASO) that is designed to boost production of the SMN protein. This therapy has the same mechanism of action as Spinraza (nusinersen), ...

Living with SMA isn't just about survival, says columnist. There's also the emotional weight of preparing for the next crisis ...

Buckle up, it's going to be an incredible ride, columnist Helen Baldwin says in a letter to her 13-year-old self.

Meeting your new medical team is never easy, especially when you have a complex and rare disease like SMA, columnist Alyssa ...

Many SMA patients continue to see gains in motor function with long-term Spinraza treatment, a real-world study from ...

Genetic testing also can be used to identify the number of copies patients have of SMN2, another gene that acts as a “backup” to SMN1.Generally, SMA patients who have more copies of SMN2 have milder ...

Type 4. SMA type 4, the mildest form of SMA and one of the rarest, is characterized by symptoms that appear in adulthood, usually after age 35.People with this form of SMA usually do not lose the ...

Babies with SMA type 0 have severe muscle weakness, poor muscle tone, and are unable to reach age-appropriate motor skills. Severe respiratory problems are common in infants with type 0 SMA.. New ...