Modern prophylactic therapies for hereditary angioedema with C1 inhibitor deficiency (HAE-C1INH) have become increasingly prevalent in Hungary, paralleling global trends, and are proving both ...

Physical activity, while not harmful, was not significantly associated with positive outcomes in this study. Physical activity before or during pregnancy was not associated with negative ...

Once-daily treprostinil palmitil inhalation powder (TPIP) has demonstrated significant promise as a next-generation therapy for pulmonary arterial hypertension (PAH), according to positive topline ...

Amyloid transthyretin cardiomyopathy (ATTR-CM) is a progressive and life-threatening heart disease that can lead to increased ventricular wall thickness, restrictive cardiomyopathy, and heart failure.

Due to a high incidence of invasive fungal infections after treatment with first- and second-generation Bruton tyrosine kinase inhibitors (BTKis), researchers are emphasizing the importance of ...

Researchers from Iran presented the case of a patient with chronic inflammatory demyelinating polyneuropathy (CIDP) who underwent emergency umbilical herniorrhaphy and whose anesthesia was ...

The levels of sialylated N-glycans in the serum could be a novel biomarker in chronic inflammatory demyelinating polyneuropathy (CIDP), according to a new study published in the European Journal of ...

A CRISPR/Cas9-modified Janus kinase 2 (JAK2) V617F model may be useful to develop new therapies against myeloproliferative neoplasms (MPNs), showed a new study published in the International Journal ...

Global start-up activities associated with the randomized, placebo-controlled, double-blind, global phase 3 ALPHA-ORBIT trial of navenibart (STAR-0215) for the treatment of patients with hereditary ...

IgG4-related orbital disease should be considered as a possible diagnosis in cases of orbital inflammatory disease. A study characterizing orbital inflammatory disease (OID), a differential diagnosis ...

A case of copper deficiency peripheral neuropathy (CDPN) associated with Wilson disease (WD) was described recently in the journal Acta Neurologica Belgica.Although CDPN has been described and linked ...

A supratherapeutic dose of 1400 mg of vatiquinone is safe and well-tolerated in patients with Friedreich ataxia (FA), according to a new study published in the journal Clinical Pharmacology in Drug ...