Exa-cel is the first FDA-approved therapy utilizing CRISPR/Cas9, a type of gene editing technology through which patients' ...

Casgevy, now a "national priority" drug, helped kids with sickle cell and thalassemia, results which may help toward a label ...

ORLANDO, Dec. 6, 2025) Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...

Think of B12 as a tiny but mighty nutrient that helps keep growing bodies energized, focused, and ready to learn. For many families, this comes as a surprise, because B12 isn’t something we tend to ...

Melbourne researchers have made a world first breakthrough into creating blood stem cells that closely resemble those in the human body. And the discovery could soon lead to personalised treatments ...

Families pay thousands of dollars to store their children’s stem cells with the hope of a healthier future. But the cells are rarely useful, and sometimes contaminated. Anna Lazos with her son and ...

Blood stem cells have been grown in a laboratory for the first time in a breakthrough that could end the need for bone marrow donors. Currently, people suffering with conditions such as leukaemia, ...

SAN FRANCISCO (KGO) -- On Saturday, families will have an opportunity to get a super-sized look into the human body in a free, immersive experience for all ages. It's happening at the Mission Science ...