Spinal muscular atrophy affects the development of the nervous system more profoundly than was previously thought, a new ...

The first-in-human clinical study of SRP-1005, known as INSIGHTT, is expected to begin in the second quarter of 2026CAMBRIDGE, Mass.--(BUSINESS WIRE)--Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the ...

The UAE is rapidly consolidating its position as a global pharmaceutical and life sciences hub, with the national market ...

Genethon, a leading laboratory in gene therapy for rare diseases, today announced that it has entered into an exclusive, worldwide licensing agreement with AskBio, a gene therapy company wholly owned ...

Initiation of the IIMPACT study follows promising Phase 1 results where Restem-L demonstrated clinically meaningful efficacy and a significant reduction in steroid use within 6 months in Idiopathic ...

The development of a brain tumor in a study participant led regulators to suspend a Hurler syndrome therapy in early testing ...

Over the next two years, the planned funding will be allocated to projects that have received some FDA feedback as well as emerging efforts.

In a world of complex gym machines, this timeless bodyweight movement remains the gold standard for developing a resilient ...

In his CEO Commentary, Frederic Revah, Ph.D., underscores the dedication, expertise and successes of Genethon's 240 scientists and professional staff as they pursue new gene therapy treatments for ...

Three current members of Florida State University’s Board of Trustees, all alumni, will remain on the panel. Here's how.

Firmly anchored in a country’s development goals. Analytical reports reflecting the World Bank Group view and aimed at engaging with government counterparts, the private sector, academia, think tanks, ...

Click here for more articles b. For Byeon Woo-seok, a Korean actor and former model currently in Milan for a fashion show ...