This test is used to diagnose myotonic muscular dystrophy, which causes muscles to stay contracted for an abnormally long time. Facioscapulohumeral muscular dystrophy (FSH MD) begins in adolescence or ...

Sanofi has added to its rare disease pipeline by licensing an antibody-RNA conjugate (ARC) for facioscapulohumeral muscular dystrophy (FSHD), a genetic muscle disorder, from US biotech miRecule.

Data from DELIVER and ACHIEVE Clinicals Trial to be Presented -- Presentation on ACHIEVE Trial in DM1 and Company Symposium to Feature Data on ...

Johnny Quintana’s life changed at the age of 19 when he was diagnosed with a rare form of muscular dystrophy called Facioscapulohumeral muscular dystrophy (FSHD).

CIS, Checklist Individual Strength FSHD, facioscapulohumeral muscular dystrophy HMSN-I, hereditary motor and sensory neuropathy type I MD, adult onset myotonic dystrophy SF-36, 36 item short form ...

candidate for myotonic dystrophy type 1 (DM1), and del-brax for facioscapulohumeral muscular dystrophy (FSHD). All three candidates are based on the same TfR1-targeting antibody component.

Duchenne muscular dystrophy (DMD) is caused by mutations in the dystrophin gene, leading to muscle degeneration. Current treatments focus on maintaining muscle function, with emerging gene ...

The Janus Henderson Global Life Sciences Fund returned -11.16% and the MSCI World Health Care IndexSM returned -11.40%. Click ...