A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...

With a shared purpose, we can realize the true promise of CRISPR and improve healthcare, providing hope to more patients with ...

Gene therapy holds the promise of preventing and curing disease by manipulating gene expression within a patient's cells.

The new workflow was adapted from an enzymatic DNA tagging technology, DNA-TAG, previously developed in the Devaraj lab. In ...

Life Biosciences is pushing cellular rejuvenation into the clinic with ER-100, an experimental gene ...

University of California San Diego-led team has discovered that restoring a key cardiac protein called connexin‑43 in a mouse ...

We know the genes, but not their functions—to resolve this long-standing bottleneck in microbial research, a joint research team has proposed a cutting-edge research strategy that leverages artificial ...

DFNB16, a recessive form of mild-to-moderate human deafness, is caused by mutations in the STRC gene, which encodes stereocilin, a protein essential for the effective function of outer hair cells as ...

Researchers found that paired pathogenic variants can restore protein function rather than make it worse. This phenomenon ...

Detailed price information for Ultragenyx Pharmaceu (RARE-Q) from The Globe and Mail including charting and trades.

Two related studies from the University of California, Riverside, have reported that reduced activity of the PTPN2 gene ...