Analysis from continued follow-up of Phase 1/2 clinical trial data in Hunter syndrome (MPS II) reinforces potential for tividenofusp alfa (DNL310) to address full disease spectrumLaunch readiness ...

Researchers at IIT Bombay have developed a simpler and more efficient method to recover immune cells grown in the lab for T-cell–based cancer therapies ...

Over the past four decades, rare disease drug development has evolved from a scientific aspiration into a central pillar of biopharmaceutical innovation. Regulatory reforms, scientific breakthroughs, ...

Over the past two decades, researchers have learned that DNA inside the cell nucleus naturally folds into a network of ...