Findings from DEVOTE support clinical benefits of the high-dose regimen of nusinersen (50 mg and 28 mg) in both ...

Treatment with a high-dose regimen of Spinraza safely improved motor function in children with SMA, according to data from the DEVOTE trial.

SK Telecom today marked the six-month anniversary of Haein, its GPU cluster built for GPUaaS, launched on August 1, 2025, designed to support large-scale AI workloads and the development of advanced ...

‘Like Jesy Nelson’s twins, I have SMA. I want to show you can live a full life and be disabled’ - Kelly Gordon, 36, was ...

A phase 2a trial of NMD Pharma’s rare disease prospect ignaseclant has missed its primary endpoint. | A phase 2a trial of NMD ...

A Midland mum living with Spinal Muscular Atrophy says she 'wouldn't trade her disability' ...

This report provides an in-depth analysis of the Cell and Gene Therapy industry, highlighting key company revenues, ...

Jesy Nelson knows more than most about the negative side of social media. The former Little Mix star has faced a torrent of ...

MIAMI, FL / ACCESS Newswire / February 4, 2026 / Bebuzee Inc. ($BBUZ), the rapidly evolving next-generation super app company, today announced a strategic sequence of major platform updates scheduled ...

Exploratory Phase 2a study showed consistent and clinically meaningful functional improvements across muscle strength, motor performance, and patient-reported outcomes in patients with ...