For boys who start corticosteroids for DMD, being taller is tied with slower growth, and being older is tied to more weight ...

Satellos Bioscience is planning a Phase 2 trial in the U.S. to test SAT-3247 in children with Duchenne who are able to walk.

Adaptive clothing for Duchenne muscular dystrophy offers comfort, ease, and independence for those with muscle weakness and ...

The U.S. Food and Drug Administration (FDA) has granted orphan drug status to NS-051/NCNP-04, an exon-skipping therapy ...

The FDA has granted orphan drug designation to CRD-003, an investigational gene therapy for limb-girdle muscular dystrophy ...

Columnist Robin Stemple didn't pay much attention to a random bug bite at first, but his situation dramatically worsened.

Columnist Patrick Moeschen shares what he wishes doctors understood about treating patients with rare diseases such as ...

In recognition of Duchenne Muscular Dystrophy Awareness Month in September, the Duchenne Muscular Dystrophy Community Spotlight campaign features a series of stories highlighting the real-life ...

A combined regimen of testosterone and growth hormone improves muscle mass, strength, and mobility in men with FSHD, a study ...

In recognition of Duchenne Muscular Dystrophy Awareness Month in September, the Duchenne Muscular Dystrophy Community Spotlight campaign features a series of stories highlighting the real-life ...

Living with muscular dystrophy can be challenging, and there are considerations that must be taken into account on a day-to-basis and in certain situations to help patients manage the disease. Many ...

Exon skipping is a treatment approach for people with Duchenne muscular dystrophy (DMD) that, while not a cure, may help to make the effects of the genetic disease less severe. Duchenne, the most ...