Zilganersen is an investigational antisense oligonucleotide designed to block the product of excess GFAP caused by mutations in the GFAP gene.

The Food and Drug Administration (FDA) has accepted for Priority Review the New Drug Application (NDA) for baxdrostat for the add-on treatment of uncontrolled or treatment resistant hypertension in ...

ST-503 is a one-time dose, investigational epigenetic regulator that specifically targets and silences the SCN9A gene.

While the International Agency for Research on Cancer labels talc that may contain asbestos as “probably carcinogenic,” the mineral continues to fall under the FDA’s Generally Recognized As Safe (GRAS ...

HealthDay News — A growing list of pots and pans is now considered unsafe, and the US Food and Drug Administration (FDA) is urging people to check their kitchens and get rid of them right away. In a ...

Earlier this year, Abraham urged Louisiana Senator Dr Bill Cassidy, a gastroenterologist who strongly supports childhood vaccines, to confirm Robert F. Kennedy Jr. as health secretary. The 2 men later ...

HealthDay News — Early use of higher-efficacy therapies is recommended for patients with moderately to severely active Crohn disease (CD), according to a living clinical practice guideline issued by ...

If approved, the new autoinjector formulation would allow patients to administer furosemide at home reducing administration time from 5 hours to under 10 seconds.

Tinlarebant is a novel oral therapy designed to reduce the build-up of bisretinoids, vitamin A-based toxins that lead to retinal complications in STGD1.

The Food and Drug Administration (FDA) has granted Breakthrough Therapy designation to olezarsen as an adjunct to diet to reduce triglyceride (TG) levels in adults with severe hypertriglyceridemia (TG ...

HealthDay News — Obstructive sleep apnea (OSA) seems to be an independent risk factor for development of Parkinson disease, and early use of continuous positive airway pressure (CPAP) could modify the ...

HealthDay News — Women with persistent thyroid hormone imbalance across pregnancy may have an increased risk of having children with autism spectrum disorder (ASD), according to a study published ...