The Muscular Dystrophy Association's agenda at its 2026 MDA Clinical & Scientific Conference in March will focus on groundbreaking research.
As a seasoned professional, columnist Patrick Moeschen “muscles through” everyday challenges — despite the irony.
Brogidirsen shows motor benefits and safety over 3.5 years of treatment in people with DMD who are amenable to exon 44 ...
Three boys with DMD given the gene therapy GNT0004 in a trial showed sustained improvements in motor function after two years ...
Columnist Shalom Lim and his girlfriend, Amanda, were among the disability advocates who let their voices be heard at a ...
Health Canada approved Agamree (vamorolone) to treat Duchenne muscular dystrophy (DMD) in patients ages 4 and older.
By grounding himself in the reasons why he keeps moving forward, columnist Patrick Moeschen is able to figure out how to ...
Avidity's exon-skipping therapy del-zota led to functional gains for people with DMD, regardless of their walking abilities, ...
Feeling discouraged by the progression of his FSHD, columnist Robin Stemple focuses on the love and kind gestures he's recently received.
Columnist Betty Vertin's sons with Duchenne MD have seen their social circle shrink over the years, but they now enjoy time with each other.
Exon skipping is a treatment approach for people with Duchenne muscular dystrophy (DMD) that, while not a cure, may help to make the effects of the genetic disease less severe. Duchenne, the most ...
Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...