Guest Voice: Moving, literally, in the right direction for sickle cell care. Richard Bayliss is 44 years old and has sickle cell disease with hemoglobin SS disease.

2 天之前 · The Phase 1 study (NCT05904093) is sponsored by the National Heart, Lung, and Blood Institute (NHLBI), part of the National Institutes of Health (NIH), and will be conducted at …

2022年1月4日 · Sickle cell disease (SCD) is an inherited disorder caused by a mutation in the gene encoding a subunit of hemoglobin, the protein that carries oxygen in red blood cells. …

6 天之前 · New treatments and therapies are being developed every day for people with sickle cell disease. I take hydroxycarbamide daily. The medicine was initially designed for cancer …

2024年12月12日 · Vertex Pharmaceuticals, which developed Casgevy alongside CRISPR Therapeutics, shared the findings at the 66 th American Society of Hematology (ASH) Annual …

2023年12月12日 · That’s according to new data from Lyfgenia’s developer, Bluebird Bio, at the 65th American Society of Hematology (ASH) Annual Meeting and Exposition.Also known as …

Sickle cell anemia is an inherited blood disorder. It is caused by a mutation in the gene encoding for hemoglobin, the protein in red blood cells that binds to oxygen so it can be transported …

2025年1月8日 · Complications vary from person to person. While numerous potential complications are associated with sickle cell disease, it’s important to note that not every …

Sickle Cell Disease News is a digital platform intended to provide the sickle cell disease (SCD) community with the most recent news and information on SCD, as well as first-hand …

2024年11月18日 · The extensive research, funding, and other resources required for gene therapy to be approved and for a patient to complete treatment can’t be understated.It also …